Research projects needed to discover interventions for rare neurodegenerative diseases are often complex and expensive. There are no proven therapies for MEPAN, but we are doing everything we can to change that. Current projects that need support and funding include:

 

• An expanded drug repurposing project with Perlara.​

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• Experiments at the University of Florida, Children's Hospital of Philadelphia and the University of Oulu to test an AAV gene therapy that may help address vision or movement issues.​

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• Developing biomarkers that may help measure MEPAN progression and the effect of any therapies over time.

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Make a donation to help advance these projects.

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